Doctors first behaved with a child with personalized gene -editing therapy for the first time

by SkillAiNest

A team of doctors and scientists for the first time successfully treated a rare genetic condition with personalized gene editing therapy. Have been the results of ground treatment I New England Journal of MedicineTogether with A doctor who previously monitored the FDA’s gene therapy regulation efforts.

Patient in this historical KJ, CPS1 was a newborn baby, which has about 50 % mortality rate within the first week. Patients who survive may experience mental illness, mental and developmental delays, and liver transplant. The maintenance team developed a personal treatment for amending the CIRCPR -based gene, which is a technology to modify human DNA.

The repair of a successful gene for KJ for the previous year’s previous federal financing medical research, including the discovery of the CRISPR and the human genome continuity, could identify the change.

This approach to modification of gene can potentially be used to help other genetic disorders, such as scale cell disease, cystic fibrosis, Huntington’s disease and muscle dystrophy patients in the future. A couple of CIRSPR -based drugs have already been received to treat scale cell diseases, but there is still much to find in this field.

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